What Role Do Orphan Drug Policies Play in Leigh Syndrome Treatment...

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2026-01-29 11:46:43 - Translate -

What Role Do Orphan Drug Policies Play in Leigh Syndrome Treatment Market Growth?

Leigh Syndrome, also known as Leigh disease, is a rare, progressive, and debilitating neurodegenerative disorder primarily affecting infants and young children. Characterized by defects in mitochondrial energy production, the syndrome leads to severe neurological dysfunction, muscle weakness, developmental delays, and respiratory complications. Due to its genetic and metabolic complexity,...

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